ISIS Pharmecuticals announces testing of new Drug to Treat Myotonic Dystrophy.
If you have this disease call you local research center and ask to be added to list of potential patients if you want to participate.
Isis Pharmaceuticals Initiates Phase 1/2 Study of ISIS-DMPK Rx in Patients With Myotonic Dystrophy Type 1
ISIS-DMPK Rx Extends the Targeting of Antisense Drugs to Include Muscle Tissue
CARLSBAD, Calif., Dec. 16, 2014 /PRNewswire/ – Isis Pharmaceuticals, Inc. (NASDAQ: ISIS) announced today that it has initiated a study for ISIS-DMPKRx in patients with Myotonic Dystrophy Type 1 (DM1). DM1 is a rare genetic neuromuscular disease caused by the production of toxic dystrophia myotonica-protein kinase (DMPK) RNA in cells. ISIS-DMPKRx is specifically designed to reduce toxic DMPK RNA.
This week ISIS pharmaceuticals announced the commencement of recruiting for Phase I of the Myotonic Dystrophy Drug Trial. This is tremendous news for the myotonic dystrophy community. The promise of scientific research to define the DNA site, identify the cause of the disease, then begin to develop treatments that would reverse the problems in the cell are culminating to the promise of hope for all that suffer from this horrible affliction.
If you want to participate in this study you must act quickly and contact the centers that are conducting the research. Find the closest location and contact the person via email or phone. You must meet all (meaning all) the qualifications for the trial. The full information is on CLINICALTRIALS
Happy Days! A clinical Trial is going to start on Phase one of Myotonic Dystrophy Drug. That means that a small number of patients in the US usually under 50 will get a chance to try the drug. The purpose of the Phase I trial is to
Try out the drug
Find an optimum dose
Assess Safety of Drug
More on what a phases of clinical testing mean (From MD Anderson site)
What are Phase 1 Clinical Trials?
Okay lots of hype on the Isis Drug that was supposed to be in early stage trials this year in actual human beings. To us waiting January 1st is a good day to start. Now we are in JUNE! Yo Isis! We are waiting patiently.
I would imagine (hopefully) the results of the lab test have been so incredibly positive that they had to delay a few months to contain their joy at what a great drug they developed………. Hopefully not the converse.
We are waiting Isis for the good news. Drop us a good news bomb!